A fragmented adeno-associated viral dual vector strategy for treatment of diseases caused by mutations in large genes leads to expression of hybrid transcripts. (2016)

First Author: McClements ME
Attributed to:  Developing gene therapy to treat blindness caused by Stargardt Disease funded by MRC

Abstract

No abstract provided

Bibliographic Information

Digital Object Identifier: http://dx.doi.org/10.4172/2157-7412.1000311

PubMed Identifier: 28239514

Publication URI: http://europepmc.org/abstract/MED/28239514

Type: Journal Article/Review

Volume: 7

Parent Publication: Journal of genetic syndromes & gene therapy

Issue: 5

ISSN: 2157-7412