Nusinersen versus Sham Control in Infantile-Onset Spinal Muscular Atrophy (2017)

Abstract

No abstract provided

Bibliographic Information

Digital Object Identifier: http://dx.doi.org/10.1056/nejmoa1702752

PubMed Identifier: 29091570

Publication URI: http://europepmc.org/abstract/MED/29091570

Type: Journal Article/Review

Parent Publication: New England Journal of Medicine

Issue: 18

ISSN: 0028-4793