Maintenance of quality of life in adults with type 1 Gaucher disease previously stabilized on enzyme therapy who were switched to oral eliglustat: 4 year results of the ENCORE trial (2017)

Bibliographic Information

Digital Object Identifier: http://dx.doi.org/10.1016/j.ymgme.2016.11.071

Publication URI: http://dx.doi.org/10.1016/j.ymgme.2016.11.071

Type: Journal Article/Review

Parent Publication: Molecular Genetics and Metabolism

Issue: 1-2