Encore - a Randomized, Controlled, Open-Label Non-Inferiority Study Comparing Eliglustat to Imiglucerase in Gaucher Disease Type 1 Patients Stabilized on Enzyme Replacement Therapy: 24-Month Results (2014)

First Author: Rosenbloom B

Attributed to: Predictive measures to stratify clinical outcomes in children and adults with Gaucher disease and responses to specific therapies funded by MRC

No abstract provided

Type: Journal Article/Review

Parent Publication: Blood

Issue: 21