A two part, multi-centre, multiple dose study of Erythrocyte Encapsulated Thymidine Phosphorylase (EETP) in patients with Mitochondrial Neurogastrointestinal Encephalomyopathy (MNGIE) (2017)

Abstract

No abstract provided

Bibliographic Information

Digital Object Identifier: http://dx.doi.org/10.1016/s0960-8966(17)30281-x

Publication URI: http://www.nmd-journal.com/article/S0960-8966(17)30281-X/abstract

Type: Journal Article/Review

Parent Publication: Neuromuscular Disorders