A novel adeno-associated virus capsid with enhanced neurotropism corrects a lysosomal transmembrane enzyme deficiency. (2018)

First Author: Tordo J
Attributed to:  The development of gene therapy for Niemann-Pick type C disease funded by MRC

Abstract

No abstract provided

Bibliographic Information

Digital Object Identifier: http://dx.doi.org/10.1093/brain/awy126

PubMed Identifier: 29788236

Publication URI: http://europepmc.org/abstract/MED/29788236

Type: Journal Article/Review

Volume: 141

Parent Publication: Brain : a journal of neurology

Issue: 7

ISSN: 0006-8950