The oral splicing modifier RG7800 increases full length survival of motor neuron 2 mRNA and survival of motor neuron protein: Results from trials in healthy adults and patients with spinal muscular atrophy. (2019)
Abstract
No abstract provided
Bibliographic Information
Digital Object Identifier: http://dx.doi.org/10.1016/j.nmd.2018.10.001
PubMed Identifier: 30553700
Publication URI: http://europepmc.org/abstract/MED/30553700
Type: Journal Article/Review
Volume: 29
Parent Publication: Neuromuscular disorders : NMD
Issue: 1
ISSN: 0960-8966