Progranulin AAV gene therapy for frontotemporal dementia: translational studies and phase 1/2 trial interim results. (2024)
Abstract
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Bibliographic Information
Digital Object Identifier: http://dx.doi.org/10.1038/s41591-024-02973-0
PubMed Identifier: 38745011
Publication URI: http://europepmc.org/abstract/MED/38745011
Type: Journal Article/Review
Volume: 30
Parent Publication: Nature medicine
Issue: 5
ISSN: 1078-8956