Peptide-conjugated oligonucleotides evoke long-lasting myotonic dystrophy correction in patient-derived cells and mice. (2019)

First Author: Klein AF
Attributed to:  Advanced peptide-oligonucleotide therapy for Myotonic Dystrophy Type 1 funded by MRC

Abstract

No abstract provided

Bibliographic Information

Digital Object Identifier: http://dx.doi.org/10.1172/jci128205

PubMed Identifier: 31479430

Publication URI: http://europepmc.org/abstract/MED/31479430

Type: Journal Article/Review

Volume: 129

Parent Publication: The Journal of clinical investigation

Issue: 11

ISSN: 0021-9738