Lentiviral Hematopoietic Stem Cell Gene Therapy Rescues Clinical Phenotypes in a Murine Model of Pompe Disease. (2020)

First Author: Piras G
Attributed to:  Tracking hydrogel therapeutics using quantitative whole-body imaging funded by MRC

Abstract

No abstract provided

Bibliographic Information

Digital Object Identifier: http://dx.doi.org/10.1016/j.omtm.2020.07.001

PubMed Identifier: 32775491

Publication URI: http://europepmc.org/abstract/MED/32775491

Type: Journal Article/Review

Volume: 18

Parent Publication: Molecular therapy. Methods & clinical development

ISSN: 2329-0501