A Novel Small NPC1 Promoter Enhances AAV-Mediated Gene Therapy in Mouse Models of Niemann-Pick Type C1 Disease. (2023)
Attributed to:
Gene therapy for Childhood Parkinsonism: Dopamine transporter deficiency syndrome
funded by
MRC
Abstract
No abstract provided
Bibliographic Information
Digital Object Identifier: http://dx.doi.org/10.3390/cells12121619
PubMed Identifier: 37371089
Publication URI: http://europepmc.org/abstract/MED/37371089
Type: Journal Article/Review
Volume: 12
Parent Publication: Cells
Issue: 12
ISSN: 2073-4409