Eliglustat maintains long-term clinical stability in patients with Gaucher disease type 1 stabilized on enzyme therapy (2017)

First Author: Cox T
Attributed to:  Gene Therapy for Tay-Sachs and Sandhoff diseases funded by MRC

Abstract

No abstract provided

Bibliographic Information

Digital Object Identifier: http://dx.doi.org/10.17863/cam.9100

Publication URI: https://www.repository.cam.ac.uk/handle/1810/263735

Type: Journal Article/Review