ENCORE, a randomized, controlled, open-label non-inferiority study comparing eliglustat to imiglucerase in Gaucher disease type 1 patients stabilized on enzyme replacement therapy: 24-month results (2015)

First Author: Cox T
Attributed to:  Gene Therapy for Tay-Sachs and Sandhoff diseases funded by MRC

Abstract

No abstract provided

Bibliographic Information

Digital Object Identifier: http://dx.doi.org/10.1016/j.ymgme.2014.12.058

Publication URI: http://dx.doi.org/10.1016/j.ymgme.2014.12.058

Type: Journal Article/Review

Parent Publication: Molecular Genetics and Metabolism

Issue: 2

ISSN: 1096-7192