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Eliglustat maintains long-term clinical stability in patients with Gaucher disease type 1 stabilized on enzyme therapy. (2017)

First Author: Cox TM

Attributed to: Gene Therapy for Tay-Sachs and Sandhoff diseases funded by MRC

Abstract

No abstract provided

Bibliographic Information

Digital Object Identifier: http://dx.doi.org/10.1182/blood-2016-12-758409

PubMed Identifier: 28167660

Publication URI: http://europepmc.org/abstract/MED/28167660

Type: Journal Article/Review

Volume: 129

Parent Publication: Blood

Issue: 17

ISSN: 0006-4971