Eliglustat maintains long-term clinical stability in patients with Gaucher disease type 1 stabilized on enzyme therapy. (2017)
Attributed to:
Gene Therapy for Tay-Sachs and Sandhoff diseases
funded by
MRC
Abstract
No abstract provided
Bibliographic Information
Digital Object Identifier: http://dx.doi.org/10.1182/blood-2016-12-758409
PubMed Identifier: 28167660
Publication URI: http://europepmc.org/abstract/MED/28167660
Type: Journal Article/Review
Volume: 129
Parent Publication: Blood
Issue: 17
ISSN: 0006-4971