AAV-mediated liver-directed gene therapy for Acute Intermittent Porphyria: It is safe but is it effective? (2016)

First Author: Brunetti-Pierri N

Abstract

No abstract provided

Bibliographic Information

Digital Object Identifier: http://dx.doi.org/10.1016/j.jhep.2016.07.006

PubMed Identifier: 27422751

Publication URI: http://europepmc.org/abstract/MED/27422751

Type: Journal Article/Review

Parent Publication: Journal of Hepatology

Issue: 4

ISSN: 0168-8278