AAV9 intracerebroventricular gene therapy improves lifespan, locomotor function and pathology in a mouse model of Niemann-Pick type C1 disease. (2018)
Attributed to:
The development of gene therapy for Niemann-Pick type C disease
funded by
MRC
Abstract
No abstract provided
Bibliographic Information
Digital Object Identifier: http://dx.doi.org/10.1093/hmg/ddy212
PubMed Identifier: 29878115
Publication URI: http://europepmc.org/abstract/MED/29878115
Type: Journal Article/Review
Volume: 27
Parent Publication: Human molecular genetics
Issue: 17
ISSN: 0964-6906