Interventions Targeting Glucocorticoid-Krüppel-like Factor 15-Branched-Chain Amino Acid Signaling Improve Disease Phenotypes in Spinal Muscular Atrophy Mice. (2018)
Attributed to:
Peptide conjugated oligonucleotides for splice switching therapy of Spinal Muscular Atrophy
funded by
MRC
Abstract
No abstract provided
Bibliographic Information
Digital Object Identifier: http://dx.doi.org/10.1016/j.ebiom.2018.04.024
PubMed Identifier: 29735415
Publication URI: http://europepmc.org/abstract/MED/29735415
Type: Journal Article/Review
Volume: 31
Parent Publication: EBioMedicine
ISSN: 2352-3964