Nusinersen versus Sham Control in Infantile-Onset Spinal Muscular Atrophy. (2017)
Abstract
No abstract provided
Bibliographic Information
Digital Object Identifier: http://dx.doi.org/10.1056/nejmoa1702752
PubMed Identifier: 29091570
Publication URI: http://europepmc.org/abstract/MED/29091570
Type: Journal Article/Review
Volume: 377
Parent Publication: The New England journal of medicine
Issue: 18
ISSN: 0028-4793