Gene therapy for Wiskott-Aldrich syndrome in a severely affected adult. (2017)
Attributed to:
Phase I/II trial of lentiviral vector mediated gene therapy for Adenosine Deaminase deficiency
funded by
MRC
Abstract
No abstract provided
Bibliographic Information
Digital Object Identifier: http://dx.doi.org/10.1182/blood-2017-04-777136
PubMed Identifier: 28716862
Publication URI: http://europepmc.org/abstract/MED/28716862
Type: Journal Article/Review
Volume: 130
Parent Publication: Blood
Issue: 11
ISSN: 0006-4971