Peptide-conjugated oligonucleotides evoke long-lasting myotonic dystrophy correction in patient-derived cells and mice. (2019)
Attributed to:
Advanced peptide-oligonucleotide therapy for Myotonic Dystrophy Type 1
funded by
MRC
Abstract
No abstract provided
Bibliographic Information
Digital Object Identifier: http://dx.doi.org/10.1172/jci128205
PubMed Identifier: 31479430
Publication URI: http://europepmc.org/abstract/MED/31479430
Type: Journal Article/Review
Volume: 129
Parent Publication: The Journal of clinical investigation
Issue: 11
ISSN: 0021-9738