Neonatal brain-directed gene therapy rescues a mouse model of neurodegenerative CLN6 Batten disease. (2019)

First Author: Kleine Holthaus SM
Attributed to:  The development of gene therapy for Niemann-Pick type C disease funded by MRC

Abstract

No abstract provided

Bibliographic Information

Digital Object Identifier: http://dx.doi.org/10.1093/hmg/ddz210

PubMed Identifier: 31807779

Publication URI: http://europepmc.org/abstract/MED/31807779

Type: Journal Article/Review

Volume: 28

Parent Publication: Human molecular genetics

Issue: 23

ISSN: 0964-6906