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Safety and efficacy of deferiprone for pantothenate kinase-associated neurodegeneration: a randomised, double-blind, controlled trial and an open-label extension study. (2019)

First Author: Klopstock T

Attributed to: Exosomal protein deficiencies: how abnormal RNA metabolism results in childhood-onset neurological diseases funded by MRC

Abstract

No abstract provided

Bibliographic Information

Digital Object Identifier: http://dx.doi.org/10.1016/s1474-4422(19)30142-5

PubMed Identifier: 31202468

Publication URI: http://europepmc.org/abstract/MED/31202468

Type: Journal Article/Review

Volume: 18

Parent Publication: The Lancet. Neurology

Issue: 7

ISSN: 1474-4422