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Fetal gene therapy for neurodegenerative lysosomal storage diseases. (2019)

First Author: Baruteau J

Attributed to: Development of rAAV-mediated gene therapy for a severe paediatric metabolic liver disease: Ornithine Transcarbamylase deficiency. funded by MRC

Abstract

No abstract provided

Bibliographic Information

Digital Object Identifier: http://dx.doi.org/10.1002/jimd.12018

PubMed Identifier: 30715735

Publication URI: http://europepmc.org/abstract/MED/30715735

Type: Journal Article/Review

Volume: 42

Parent Publication: Journal of inherited metabolic disease

Issue: 3

ISSN: 0141-8955