Gene therapy for global brain diseases: one small step for mice, one giant leap for humans. (2020)

First Author: Rahim AA
Attributed to:  The development of gene therapy for Niemann-Pick type C disease funded by MRC

Abstract

No abstract provided

Bibliographic Information

Digital Object Identifier: http://dx.doi.org/10.1093/brain/awaa189

PubMed Identifier: 32671401

Publication URI: http://europepmc.org/abstract/MED/32671401

Type: Journal Article/Review

Volume: 143

Parent Publication: Brain : a journal of neurology

Issue: 7

ISSN: 0006-8950