Correction of amyotrophic lateral sclerosis related phenotypes in induced pluripotent stem cell-derived motor neurons carrying a hexanucleotide expansion mutation in C9orf72 by CRISPR/Cas9 genome editing using homology-directed repair. (2020)

First Author: Ababneh NA
Attributed to:  Identifying effectors of mutant C9Orf72 ALS/FTD to combat neurodegeneration funded by MRC

Abstract

No abstract provided

Bibliographic Information

Digital Object Identifier: http://dx.doi.org/10.1093/hmg/ddaa106

PubMed Identifier: 32504093

Publication URI: http://europepmc.org/abstract/MED/32504093

Type: Journal Article/Review

Volume: 29

Parent Publication: Human molecular genetics

Issue: 13

ISSN: 0964-6906