Aromatic l -amino acid decarboxylase deficiency: a patient-derived neuronal model for precision therapies (2021)
Attributed to:
EnCRISPrx - A Permanent CRISPR-based Approach To Rescue Dravet Syndrome By Enhancing Scn1a Promoter Activity
funded by
MRC
Abstract
No abstract provided
Bibliographic Information
Digital Object Identifier: http://dx.doi.org/10.1093/brain/awab123
PubMed Identifier: 33734312
Publication URI: http://europepmc.org/abstract/MED/33734312
Type: Journal Article/Review
Parent Publication: Brain
Issue: 8
ISSN: 0006-8950