Enzyme replacement therapy and hematopoietic stem cell transplant: a new paradigm of treatment in Wolman disease. (2021)

Abstract

No abstract provided

Bibliographic Information

Digital Object Identifier: http://dx.doi.org/10.1186/s13023-021-01849-7

PubMed Identifier: 34020687

Publication URI: http://europepmc.org/abstract/MED/34020687

Type: Journal Article/Review

Volume: 16

Parent Publication: Orphanet journal of rare diseases

Issue: 1

ISSN: 1750-1172