📣 Help Shape the Future of UKRI's Gateway to Research (GtR)

We're improving UKRI's Gateway to Research and are seeking your input! If you would be interested in being interviewed about the improvements we're making and to have your say about how we can make GtR more user-friendly, impactful, and effective for the Research and Innovation community, please email gateway@ukri.org.

Maintenance of quality of life in adults with type 1 Gaucher disease previously stabilized on enzyme therapy who were switched to oral eliglustat: 4 year results of the ENCORE trial (2017)

First Author: Cox T

Attributed to: Predictive measures to stratify clinical outcomes in children and adults with Gaucher disease and responses to specific therapies funded by MRC

Abstract

No abstract provided

Bibliographic Information

Digital Object Identifier: http://dx.doi.org/10.1016/j.ymgme.2016.11.071

Publication URI: http://dx.doi.org/10.1016/j.ymgme.2016.11.071

Type: Journal Article/Review

Parent Publication: Molecular Genetics and Metabolism

Issue: 1-2