Gene therapy restores dopamine transporter expression and ameliorates pathology in iPSC and mouse models of infantile parkinsonism (2021)

First Author: Ng Joanne

Attributed to: EnCRISPrx - A Permanent CRISPR-based Approach To Rescue Dravet Syndrome By Enhancing Scn1a Promoter Activity funded by MRC

No abstract provided

Type: Journal Article/Review

Volume: 13

Parent Publication: SCIENCE TRANSLATIONAL MEDICINE

Issue: 594

ISSN: 1946-6234