Gene Therapy Targeting the Inner Retina Rescues the Retinal Phenotype in a Mouse Model of CLN3 Batten Disease. (2020)

First Author: Kleine Holthaus SM
Attributed to:  The development of gene therapy for Niemann-Pick type C disease funded by MRC

Abstract

No abstract provided

Bibliographic Information

Digital Object Identifier: http://dx.doi.org/10.1089/hum.2020.038

PubMed Identifier: 32578444

Publication URI: http://europepmc.org/abstract/MED/32578444

Type: Journal Article/Review

Volume: 31

Parent Publication: Human gene therapy

Issue: 13-14

ISSN: 1043-0342