Muscle overexpression of Klf15 via an AAV8-Spc5-12 construct does not provide benefits in spinal muscular atrophy mice. (2019)
Attributed to:
Peptide conjugated oligonucleotides for a phase I/IIa clinical trial in Spinal Muscular Atrophy
funded by
MRC
Abstract
No abstract provided
Bibliographic Information
Digital Object Identifier: http://dx.doi.org/10.1038/s41434-020-0146-8
PubMed Identifier: 32313099
Publication URI: http://europepmc.org/abstract/MED/32313099
Type: Journal Article/Review
Volume: 27
Parent Publication: Gene therapy
Issue: 10-11
ISSN: 0969-7128