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Venglustat combined with imiglucerase for neurological disease in adults with Gaucher disease type 3: the LEAP trial (2023)

First Author: Schiffmann R

Attributed to: Predictive measures to stratify clinical outcomes in children and adults with Gaucher disease and responses to specific therapies funded by MRC

Abstract

No abstract provided

Bibliographic Information

Digital Object Identifier: http://dx.doi.org/10.1093/brain/awac379

PubMed Identifier: 36256599

Publication URI: http://europepmc.org/abstract/MED/36256599

Type: Journal Article/Review

Parent Publication: Brain

Issue: 2

ISSN: 0006-8950