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Three-Country Snapshot of Ornithine Transcarbamylase Deficiency. (2022)

First Author: Seker Yilmaz B

Attributed to: Phase I/II clinical trial evaluating AAV-mediated gene therapy for a severe paediatric metabolic liver disease: Ornithine Transcarbamylase deficiency funded by MRC

Abstract

No abstract provided

Bibliographic Information

Digital Object Identifier: http://dx.doi.org/10.3390/life12111721

PubMed Identifier: 36362876

Publication URI: http://europepmc.org/abstract/MED/36362876

Type: Journal Article/Review

Volume: 12

Parent Publication: Life (Basel, Switzerland)

Issue: 11

ISSN: 2075-1729