📣 Help Shape the Future of UKRI's Gateway to Research (GtR)

We're improving UKRI's Gateway to Research and are seeking your input! If you would be interested in being interviewed about the improvements we're making and to have your say about how we can make GtR more user-friendly, impactful, and effective for the Research and Innovation community, please email gateway@ukri.org.

Long-term effects of eliglustat on skeletal manifestations in clinical trials of patients with Gaucher disease type 1. (2023)

First Author: Cox TM

Attributed to: Predictive measures to stratify clinical outcomes in children and adults with Gaucher disease and responses to specific therapies funded by MRC

Abstract

No abstract provided

Bibliographic Information

Digital Object Identifier: http://dx.doi.org/10.1016/j.gim.2022.10.011

PubMed Identifier: 36469032

Publication URI: http://europepmc.org/abstract/MED/36469032

Type: Journal Article/Review

Volume: 25

Parent Publication: Genetics in medicine : official journal of the American College of Medical Genetics

Issue: 2

ISSN: 1098-3600