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A cell-penetrant peptide blocking C9ORF72-repeat RNA nuclear export reduces the neurotoxic effects of dipeptide repeat proteins. (2023)

First Author: Castelli LM

Attributed to: Novel therapeutic strategies to target RAN translation of pathological C9ORF72 repeat transcripts and associated neurodegeneration funded by MRC

Abstract

No abstract provided

Bibliographic Information

Digital Object Identifier: http://dx.doi.org/10.1126/scitranslmed.abo3823

PubMed Identifier: 36857431

Publication URI: http://europepmc.org/abstract/MED/36857431

Type: Journal Article/Review

Volume: 15

Parent Publication: Science translational medicine

Issue: 685

ISSN: 1946-6234