Gene therapy with AR isoform 2 rescues spinal and bulbar muscular atrophy phenotype by modulating AR transcriptional activity (2021)
Attributed to:
Antisense Oligonucleotide Therapy for Neuromuscular Disease
funded by
MRC
Abstract
No abstract provided
Bibliographic Information
Digital Object Identifier: http://dx.doi.org/10.1126/sciadv.abi6896
PubMed Identifier: 34417184
Publication URI: http://europepmc.org/abstract/MED/34417184
Type: Journal Article/Review
Parent Publication: Science Advances
Issue: 34
ISSN: 2375-2548