Gene therapy with AR isoform 2 rescues spinal and bulbar muscular atrophy phenotype by modulating AR transcriptional activity (2021)

First Author: Lim W
Attributed to:  Antisense Oligonucleotide Therapy for Neuromuscular Disease funded by MRC

Abstract

No abstract provided

Bibliographic Information

Digital Object Identifier: http://dx.doi.org/10.1126/sciadv.abi6896

PubMed Identifier: 34417184

Publication URI: http://europepmc.org/abstract/MED/34417184

Type: Journal Article/Review

Parent Publication: Science Advances

Issue: 34

ISSN: 2375-2548