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Phase 1-2 Trial of AAVS3 Gene Therapy in Patients with Hemophilia B. (2022)

First Author: Chowdary P

Attributed to: MICA: An open label dose-escalation study of a novel adeno-associated viral vector for gene transfer in subjects with haemophilia A funded by MRC

Abstract

No abstract provided

Bibliographic Information

Digital Object Identifier: http://dx.doi.org/10.1056/nejmoa2119913

PubMed Identifier: 35857660

Publication URI: http://europepmc.org/abstract/MED/35857660

Type: Journal Article/Review

Volume: 387

Parent Publication: The New England journal of medicine

Issue: 3

ISSN: 0028-4793