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A Novel Small NPC1 Promoter Enhances AAV-Mediated Gene Therapy in Mouse Models of Niemann-Pick Type C1 Disease. (2023)

Abstract

No abstract provided

Bibliographic Information

Digital Object Identifier: http://dx.doi.org/10.3390/cells12121619

PubMed Identifier: 37371089

Publication URI: http://europepmc.org/abstract/MED/37371089

Type: Journal Article/Review

Volume: 12

Parent Publication: Cells

Issue: 12

ISSN: 2073-4409