Outcomes and Adverse Effects of Voretigene Neparvovec Treatment for Biallelic RPE65-Mediated Inherited Retinal Dystrophies in a Cohort of Patients from a Single Center. (2023)

First Author: Kiraly P
Attributed to:  Development of AAV gene therapy for blindness caused by cone-rod dystrophy funded by MRC

Abstract

No abstract provided

Bibliographic Information

Digital Object Identifier: http://dx.doi.org/10.3390/biom13101484

PubMed Identifier: 37892166

Publication URI: http://europepmc.org/abstract/MED/37892166

Type: Journal Article/Review

Volume: 13

Parent Publication: Biomolecules

Issue: 10

ISSN: 2218-273X