mRNA therapy corrects defective glutathione metabolism and restores ureagenesis in preclinical argininosuccinic aciduria. (2024)
Attributed to:
MICA: Neuronal Arginine Metabolism in Health and Disease
funded by
MRC
Abstract
No abstract provided
Bibliographic Information
Digital Object Identifier: http://dx.doi.org/10.1126/scitranslmed.adh1334
PubMed Identifier: 38198573
Publication URI: http://europepmc.org/abstract/MED/38198573
Type: Journal Article/Review
Volume: 16
Parent Publication: Science translational medicine
Issue: 729
ISSN: 1946-6234