mRNA therapy corrects defective glutathione metabolism and restores ureagenesis in preclinical argininosuccinic aciduria. (2024)

First Author: Gurung S

Abstract

No abstract provided

Bibliographic Information

Digital Object Identifier: http://dx.doi.org/10.1126/scitranslmed.adh1334

PubMed Identifier: 38198573

Publication URI: http://europepmc.org/abstract/MED/38198573

Type: Journal Article/Review

Volume: 16

Parent Publication: Science translational medicine

Issue: 729

ISSN: 1946-6234