Muscle overexpression of Klf15 via an AAV8-Spc5-12 construct does not provide benefits in spinal muscular atrophy mice (2019)

First Author: Ahlskog N

Attributed to: Peptide conjugated oligonucleotides for a phase I/IIa clinical trial in Spinal Muscular Atrophy funded by MRC

Abstract

No abstract provided

Bibliographic Information

Digital Object Identifier: http://dx.doi.org/10.1101/717785

Publication URI: http://dx.doi.org/10.1101/717785

Type: Preprint