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Donald A, Kämpe-Björkvall C, Vellodi A; GAUCHERITE Consortium; Cox TM, Hughes DA, Jones SA, Wynn R, Machaczka M (2022). Thirty- year clinical outcomes after Haematopoietic Stem Cell Transplantation in Neuronopathic Gaucher Disease. Orphanet Journal of Rare Diseases. . 2022 Jun 18;17(1):234. (2022)

First Author: Donald A

Attributed to: Predictive measures to stratify clinical outcomes in children and adults with Gaucher disease and responses to specific therapies funded by MRC

Abstract

No abstract provided

Bibliographic Information

Type: Journal Article/Review

Parent Publication: Orphanet J Rare Dis