Zaccariotto E, Cachón-González MB, Lim S, Hirth B, Park H, Fezoui M, Wang B, Sardi SP, Mason P, Barker RH Jr, Cox TM (2022). A novel brain-penetrant oral UGT8 inhibitor decreases in vivo galactosphingolipid biosynthesis in murine Krabbe disease. (2022)
Attributed to:
Gene Therapy for Tay-Sachs and Sandhoff diseases
funded by
MRC
Abstract
No abstract provided
Bibliographic Information
Type: Journal Article/Review
Parent Publication: Biomedicine and Pharmacotherapy