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CRISPR-Cas9 correction of a nonsense mutation in LCA5 rescues lebercilin expression and localization in human retinal organoids. (2023)

First Author: Afanasyeva TAV

Attributed to: Novel therapeutic approaches to rescue retinal dysfunction in patient-derived photoreceptors funded by MRC

Abstract

No abstract provided

Bibliographic Information

Digital Object Identifier: http://dx.doi.org/10.1016/j.omtm.2023.05.012

PubMed Identifier: 37305852

Publication URI: http://europepmc.org/abstract/MED/37305852

Type: Journal Article/Review

Volume: 29

Parent Publication: Molecular therapy. Methods & clinical development

ISSN: 2329-0501