CRISPR-Cas9 correction of a nonsense mutation in LCA5 rescues lebercilin expression and localization in human retinal organoids. (2023)
Attributed to:
Novel therapeutic approaches to rescue retinal dysfunction in patient-derived photoreceptors
funded by
MRC
Abstract
No abstract provided
Bibliographic Information
Digital Object Identifier: http://dx.doi.org/10.1016/j.omtm.2023.05.012
PubMed Identifier: 37305852
Publication URI: http://europepmc.org/abstract/MED/37305852
Type: Journal Article/Review
Volume: 29
Parent Publication: Molecular therapy. Methods & clinical development
ISSN: 2329-0501