Effective AAV-mediated gene replacement therapy in retinal organoids modeling AIPL1-associated LCA4 (2024)

Abstract

No abstract provided

Bibliographic Information

Digital Object Identifier: http://dx.doi.org/10.1016/j.omtn.2024.102148

Publication URI: http://dx.doi.org/10.1016/j.omtn.2024.102148

Type: Journal Article/Review

Parent Publication: Molecular Therapy - Nucleic Acids

Issue: 1