A translatable RNAi-driven gene therapy silences PMP22/Pmp22 genes and improves neuropathy in CMT1A mice. (2022)

Abstract

No abstract provided

Bibliographic Information

Digital Object Identifier: http://dx.doi.org/10.17863/cam.87081

Publication URI: https://www.repository.cam.ac.uk/handle/1810/339662

Type: Journal Article/Review