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Cell-mediated exon skipping normalizes dystrophin expression and muscle function in a new mouse model of Duchenne Muscular Dystrophy. (2024)

First Author: Galli F

Attributed to: Cell mediated gene therapy for Duchenne muscular dystrophy: trans-correction of resident nuclei to amplify dystrophin expression funded by MRC

Abstract

No abstract provided

Bibliographic Information

Digital Object Identifier: http://dx.doi.org/10.1038/s44321-024-00031-3

PubMed Identifier: 38438561

Publication URI: http://europepmc.org/abstract/MED/38438561

Type: Journal Article/Review

Volume: 16

Parent Publication: EMBO molecular medicine

Issue: 4

ISSN: 1757-4676