Eliglustat maintains long-term clinical stability in patients with Gaucher disease type 1 stabilized on enzyme therapy (2017)
Attributed to:
Gene Therapy for Tay-Sachs and Sandhoff diseases
funded by
MRC
Abstract
No abstract provided
Bibliographic Information
Digital Object Identifier: http://dx.doi.org/10.17863/cam.9100
Publication URI: https://www.repository.cam.ac.uk/handle/1810/263735
Type: Journal Article/Review